Scout | URGenT Resource Access (X01): Nonclinical & Manufacturing Support for Ultra‑Rare Gene Therapies (No Clinical Trials)

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URGenT Resource Access (X01): Nonclinical & Manufacturing Support for Ultra‑Rare Gene Therapies (No Clinical Trials)

This NINDS X01 gives investigators no-cost access to URGenT CRO/CMO resources and subject-matter experts to support planning, manufacturing, and limited nonclinical development of gene- or transcript-directed therapies for ultra-rare neurological and neuromuscular diseases (clinical trials not allowed). Awardees receive a multidisciplinary project team to develop IND-enabling activities, prepa…

Source

Agency: National Institutes of Health

Sub-agency: National Institute of Neurological Disorders and Stroke

Dates

Opportunity Released: December 18, 2024

Eligibility

government

individual

industry:manufacturing

industry:research

nonprofit

small_business

tribal

university

Higher Education Institutions: Private Institutions of Higher Education

Nonprofits without 501(c)(3) IRS Status (Other than Institutions of Higher Education)

For-Profit Organizations (Other than Small Businesses)

City or Township Governments

Native American Tribal Organizations (other than Federally recognized tribal governments)

Keywords

ultra-rare

gene-therapy

ind-enabling

nonclinical

manufacturing

oligonucleotide

viral-vectors

precision-therapeutics

Supporting Links

Documents

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